What is Farber Disease?
As a very rare genetic disease with patients spread out around the world, Farber disease is not always recognized by doctors and is often misdiagnosed as a form of arthritis.
A Doctor's Quest to Fight Farber Disease
We sat down with Dr. Solyom, Senior Vice President of Rare Disease Development at Aceragen to discuss his work with pediatric patients and their mission to bring treatments to market for patients living with Farber disease, a rare, metabolic disease often misdiagnosed as JIA.
Clinical Research in Becker Muscular Dystrophy
What is Becker Muscular Dystrophy?Muscular dystrophies are genetic disorders that result in progressive weakening...
Trial By Fire: Industry challenges and gaps between drug development and patients
In this episode, our Trial By Fire duo interviews Scott Schliebner. Scott is a clinical...
Trial By Fire: Caregiving during COVID and designing protocols for the patient
We're joined by Anne Marie Mercurio who is a Patient Research Advocate working primarily in oncology. We discuss the struggles of caregiving in the COVID-19 pandemic, listening to the patient experience and re-designing clinical trial protocol to fit patient needs.
Announcing Trial By Fire: A Limited Podcast Series
Check out our very first episode: "Wolfram syndrome, Paralympic athletes, and all things patient engagement."
Trial By Fire: Wolfram syndrome, Paralympic athletes, and all things patient engagement
The Clara Team is excited to introduce our limited podcast series: Trial by Fire, which...
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